Related by context. Frequent words. (Click for all words.) 75 Cystic fibrosis 69 Pulmonary hypertension 68 neurodegenerative disorder 68 Multiple sclerosis MS 67 progressive degenerative 66 Muscular dystrophy 65 fatal neurodegenerative 65 Major depressive disorder 64 cancer inflammation autoimmune 64 degenerative disorder 64 commercializes innovative biopharmaceuticals 63 Amyotrophic lateral sclerosis 62 AAT deficiency 62 Ulcerative colitis 62 congenital disorders 62 chronic inflammatory bowel 62 progressive neurodegenerative disease 62 Fatty liver 62 BioMarin develops 61 Chronic hepatitis B 61 muscular dystrophies 61 Peanut allergy 61 anemias 61 hereditary disorder 61 degenerative neurological disorder 61 TTR amyloidosis 61 Acromegaly 61 spinal muscular atrophy SMA 61 meningitis pneumonia 61 blood clotting disorders 61 Emphysema 61 chronic neurological disorder 60 Myelofibrosis 60 Genital herpes 60 arthritis gout 60 Malignant gliomas 60 lysosomal storage diseases 60 Anorexia nervosa 60 blood clotting disorder 60 Pre eclampsia 60 Periodontal disease 60 autosomal recessive 60 rheumatoid arthritis lupus 59 Gliomas 59 Hip fractures 59 Sickle cell 59 Congenital heart 59 genetically inherited 59 Malignant melanoma 59 Gestational diabetes 59 Peripheral neuropathy 59 Leber congenital amaurosis 59 Periodontitis 59 Irritable bowel syndrome 59 Acid reflux 59 uremia 59 neurodevelopmental disorder 59 Cystic Fibrosis CF 59 nephritis 59 Diabetes mellitus 59 Obstructive sleep apnea 58 Hemophilia B 58 content VENDOR WHITE PAPER 58 paroxysmal nocturnal hemoglobinuria 58 fatal malady 58 ataxia telangiectasia 58 Preeclampsia 58 Multiple myeloma 58 Parkinson disease Alzheimer disease 58 Inflammatory bowel disease 58 Retinopathy 58 hematopoietic cell 58 cirrhosis liver cancer 58 progressive neurological disorder 58 Toxoplasmosis 58 Oxidative stress 58 Stomach Cancer 58 Joubert syndrome 58 Fragile X Syndrome 58 neurobiological disorder 58 Diabetic retinopathy 58 Human papillomavirus 58 pattern baldness 58 dystrophy 58 DiGeorge syndrome 57 neurological disorder characterized 57 autosomal dominant 57 Mucositis 57 Polycystic Kidney Disease 57 Chronic obstructive pulmonary 57 blindness deafness 57 Usher syndrome 57 Hyperthyroidism 57 Pneumococcal disease 57 Chronic fatigue 57 clotting disorder 57 chronic relapsing 57 disease NAFLD 57 hemolytic anemia 57 epidermolysis bullosa 57 developmental abnormalities