Related by context. Frequent words. (Click for all words.) 58 orphan medicinal product 58 Orphan Drug status 55 K RAS 55 granted Orphan Drug 55 FDA Orphan Drug 54 granted Fast Track 54 R sorafenib tablets 53 Pivotal Phase III 52 Orphan Medicinal Product 52 granted orphan 52 Gemzar ® 52 PREZISTA r 52 Alemtuzumab 52 K ras 51 romiplostim 51 medium provenance 51 Amrubicin 50 KRAS gene 50 Vectibix 50 metastatic renal cell carcinoma 49 Positive Opinion 49 mCRC 49 Fibrillex TM 49 Torisel 49 orphan designation 49 Investigational Device Exemption 49 voriconazole 48 orphan drug 48 Orphan Drug designation 48 EGFR expressing metastatic colorectal 48 Lenalidomide 48 HER2 positive metastatic breast 48 diagnosed multiple myeloma 48 pegylated 48 KRAS wild 48 FDA Accepts 48 tumor lysis syndrome 47 vandetanib 47 Laquinimod 47 Everolimus 47 Marketing Authorization 47 Chronic Hepatitis C 47 Orphan Drug Status 47 Fast Track Designation 47 mRCC 47 Phase III Clinical Trial 47 nitazoxanide 47 liposomal formulation 47 allogeneic stem cell 47 metastatic castration resistant 47 FLT3 47 Bevacizumab 46 prospectively defined 46 hypercalcemia 46 acute promyelocytic leukemia APL 46 Orphan Drug 46 panitumumab 46 KRAS mutations 46 gastrointestinal stromal tumors 45 EGFR mutation 45 luteinizing hormone releasing 45 Fast Track designation 45 Secondary endpoints included 45 refractory multiple myeloma 45 docetaxel chemotherapy 45 factor receptor EGFR 45 bucindolol 45 Dasatinib 45 plus dexamethasone 45 Complete Response 45 superficial bladder cancer 44 Cethromycin 44 interferon alfa 44 randomized #:# 44 pheochromocytoma 44 FOLFIRI 44 azacitidine 44 chronic myeloid leukemia CML 44 BRAF mutation 44 Metastatic Colorectal Cancer 44 Orphan Drug Designation 44 indolent NHL 44 EGFR mutations 44 androgen independent 43 myeloid 43 IV melanoma 43 HCV genotype 43 cyclosporin 43 plus prednisone 43 B CLL 43 Patient Enrollment 43 JAK2 43 metastatic hormone refractory 43 decitabine 43 relapsed refractory 43 blinded placebo controlled 43 unresectable 43 resectable 43 CYP#C# [002] 43 sunitinib 43 bleomycin