Related by context. Frequent words. (Click for all words.) 65 Duchenne muscular dystrophy 65 neurodegenerative disease 64 Duchenne Muscular Dystrophy 63 Rett syndrome 62 cystinosis 61 Spinal Muscular Atrophy 61 neuromuscular disease 60 neurofibromatosis 60 Duchenne 60 Pompe 60 muscular dystrophy 60 cystic fibrosis 59 genetic disorder 59 neurodegeneration 59 Pompe disease 59 motor neuron disease 59 Rett Syndrome 58 cystic fibrosis CF 58 autoimmune disease 58 neurodegenerative 58 neurodegenerative diseases 57 Amyotrophic Lateral Sclerosis ALS 57 mitochondrial disease 57 Huntington Disease 57 ataxia 57 Fragile X syndrome 57 myelofibrosis 56 genetic defect 56 medulloblastoma 56 metabolic disorder 56 scleroderma 56 Fragile X 56 myasthenia gravis 56 retinoblastoma 56 retinitis pigmentosa 56 neurological diseases 55 Cystic Fibrosis 55 amyotrophic lateral sclerosis ALS 55 autoimmunity 55 systemic lupus erythematosus 55 Cystic fibrosis 55 relapsing remitting multiple sclerosis 55 progeria 55 rheumatoid arthritis 55 diabetic nephropathy 55 PTC# 55 autoimmune 55 spinal muscular atrophy 54 Hedgehog pathway 54 neuroblastoma 54 Neuroblastoma 54 acute myeloid leukemia 54 amyloidosis 54 Parkinson disease PD 54 chronic lymphocytic leukemia CLL 54 autoimmune diseases 54 inflammatory arthritis 54 neurological disorder 54 sarcomas 54 Crohn disease 54 antisense drugs 54 HDAC inhibitors 53 epilepsy 53 neurodegenerative disorders 53 diabetic macular edema 53 retinal diseases 53 juvenile diabetes 53 nephrotic syndrome 53 lupus 53 sickle cell disease 53 multiple sclerosis 53 Alzheimer disease AD 53 uveitis 53 HDAC 53 chronic autoimmune 53 inflammatory bowel disease 53 Gaucher disease 53 Age Related Macular 53 Inflammatory Bowel Disease 52 hepatocellular carcinoma 52 ALS 52 Alzheimer disease 52 lymphomas 52 Parkinson disease 52 acute myeloid leukemia AML 52 multiple myeloma 52 iron overload 52 STAT3 52 kinase inhibitor 52 multiple sclerosis MS 52 cachexia 52 ankylosing spondylitis 52 neuropsychiatric disorders 52 diabetic retinopathy 52 dilated cardiomyopathy 52 glioblastoma 52 Multiple Sclerosis MS 52 defective gene 51 immune mediated 51 CLL 51 juvenile rheumatoid arthritis