Related by context. Frequent words. (Click for all words.) 71 MPS VI 67 blood clotting disorder 66 fatal neurodegenerative 64 neurodegenerative disorder 64 degenerative disorder 64 progressive neurodegenerative disease 64 Multiple sclerosis MS 63 Ulcerative colitis 63 AAT deficiency 62 CIDP 62 hereditary disorder 62 Friedreich Ataxia 62 relapsing multiple sclerosis 61 Hemophilia B 61 progressive degenerative 61 Cushing syndrome 61 primary pulmonary hypertension 61 Osteosarcoma 61 rheumatic disease 61 paroxysmal nocturnal hemoglobinuria 60 Irritable bowel syndrome 60 Peripheral neuropathy 60 genetic disorder 60 polyneuropathy 60 mucopolysaccharidosis 60 C1 inhibitor deficiency 60 immunologic diseases 60 AA amyloidosis 60 optic neuropathy 60 Gaucher Disease 60 demyelinating disease 59 Duchenne muscular dystrophy DMD 59 phenylketonuria 59 commercializes innovative biopharmaceuticals 59 non alcoholic steatohepatitis 59 Parkinsons disease 59 Crohn disease chronic 59 hemolytic anemia 59 von Willebrand disease 59 metabolic disorder 59 glomerulonephritis 59 Fabry disease 59 immuno inflammatory diseases 59 autosomal dominant 59 Diabetes mellitus 58 muscular dystrophies 58 Levodopa 58 Cystic fibrosis 58 porphyria 58 BioMarin develops 58 systemic lupus erythematosus SLE 58 Systemic Lupus Erythematosus 58 Alemtuzumab 58 Duchenne Muscular Dystrophy DMD 58 systemic lupus erythematosus 58 Acute Myeloid Leukemia AML 58 Chronic Lymphocytic Leukemia 58 Leber congenital amaurosis 58 Behcet disease 58 fibromyalgia syndrome 58 myotonic dystrophy 58 Rheumatoid arthritis 58 cancer cachexia 58 degenerative disorders 58 Paget disease 58 Hypoactive Sexual Desire Disorder 58 Autoimmune diseases 58 myelodysplasia 57 infantile spasms 57 progressive neurological disorder 57 phenylketonuria PKU 57 Malignant gliomas 57 Neuropathic pain 57 Irritable Bowel Syndrome IBS 57 vaginitis 57 hematopoietic cell 57 Ulcerative Colitis 57 Glioma 57 postherpetic neuralgia 57 NF2 57 acne vulgaris 57 diabetic peripheral neuropathy 57 epidermolysis bullosa 57 Allergic rhinitis 57 aHUS 57 epilepsy 57 Multiple myeloma 57 idiopathic pulmonary fibrosis IPF 57 autoimmune disease 57 lupus nephritis 57 primary immunodeficiency 57 Epratuzumab 57 manic depressive illness 57 nephritis 56 rheumatoid arthritis psoriasis 56 Irinotecan 56 cytomegalovirus CMV 56 myeloproliferative disorders 56 recurrent seizures 56 Genital herpes 56 enzyme deficiency