Related by context. Frequent words. (Click for all words.) 63 Myozyme 59 cystic fibrosis 58 genetic disorder 58 muscular dystrophy 57 Duchenne muscular dystrophy 56 acute myeloid leukemia 55 Gaucher disease 54 Duchenne 52 Cystic fibrosis 52 rheumatoid arthritis 52 Fabry disease 52 neurodegenerative disease 52 multiple sclerosis 51 pulmonary arterial hypertension 50 lupus 50 multiple myeloma 50 leukemia 50 amyotrophic lateral sclerosis ALS 50 chronic myeloid leukemia 50 neuroblastoma 50 pulmonary hypertension 50 epilepsy 49 Parkinson disease 49 haemophilia 48 multiple sclerosis MS 48 Huntington Disease 48 ulcerative colitis 48 chronic lymphocytic leukemia 48 acute lymphoblastic leukemia 48 retinitis pigmentosa 48 Crohn disease 48 allergic asthma 48 acute myelogenous leukemia 47 non Hodgkin lymphoma 47 Cystic Fibrosis 47 acute leukemia 47 Alzheimer disease AD 47 related macular degeneration 46 glioblastoma 46 Alzheimer disease 46 progeria 46 rheumatoid arthritis RA 46 autism spectrum disorders 46 CLL 46 autoimmune disease 46 Fragile X 46 gene therapy 45 Cerezyme 45 Soliris 45 muscle wasting 45 psoriasis 45 spina bifida 45 HAE 45 amyotrophic lateral sclerosis 45 hemophilia 45 leukemias 45 defective gene 45 hormone refractory prostate cancer 45 cerebral palsy 44 Muscular Dystrophy 44 Fabrazyme 44 atopic dermatitis 44 pancreatic cancer 44 Rheumatoid Arthritis 44 osteoarthritis 44 Parkinson Disease 44 dwarfism 44 onset diabetes 44 Dacogen 44 sickle cell disease 44 ADHD 44 macular degeneration 44 neurological disorder 44 spinal cord injuries 43 glioblastoma multiforme 43 chronic kidney 43 scleroderma 43 renal cell carcinoma 43 psoriatic arthritis 43 liver cancer 43 chronic renal failure 43 severe sepsis 43 metastatic melanoma 43 melanoma 43 schizophrenia 43 osteosarcoma 43 arthritis 43 Rheumatoid arthritis 43 autism spectrum disorder 43 myeloma 43 sarcoma 43 PAH 43 genetic defect 43 degenerative disease 43 degenerative brain 43 celiac disease 43 dystonia 43 Gleevec 43 alemtuzumab 43 incurable disease 43 Down syndrome