Related by context. Frequent words. (Click for all words.) 68 Pulmonary hypertension 67 demyelinating disease 65 paroxysmal nocturnal hemoglobinuria 65 fatal neurodegenerative 64 blood clotting disorder 64 fatal malady 63 aseptic meningitis 62 Leber congenital amaurosis 62 meningoencephalitis 62 optic neuropathy 62 receiving VELCADE 62 Retinopathy 62 pheochromocytoma 62 Retinoblastoma 62 commercializes innovative biopharmaceuticals 61 neutropenia thrombocytopenia 61 degenerative disorder 61 unknown etiology 60 Cytomegalovirus 60 Lactic acidosis 60 neuroleptic malignant syndrome 60 glomerulonephritis 60 Asymptomatic 60 hepatic failure 60 lysosomal storage diseases 60 BioMarin develops 59 hemolytic anemia 59 lactic acidosis 59 neurodegenerative disorder 59 heparin induced thrombocytopenia 59 non alcoholic steatohepatitis 59 Thrombocytopenia 59 autosomal dominant 59 Ischemic 59 bone marrow suppression 58 progressive neurodegenerative disease 58 Ulcerative colitis 58 purpura 58 neurological complications 58 neurologic symptoms 58 Cushing syndrome 58 Multiple sclerosis MS 58 Hyperthyroidism 58 Treatable 58 hereditary disorder 58 myelodysplasia 58 carcinoid 58 progressive degenerative 58 Duchenne muscular dystrophy DMD 57 cerebrovascular accident 57 lymphoma leukemia 57 anemias 57 epidermolysis bullosa 57 paroxysmal nocturnal hemoglobinuria PNH 57 progressive multifocal leukoencephalopathy PML 57 AAT deficiency 57 Osteosarcoma 57 Hypoglycemia 57 congenital disorder 57 endocrine disorders 57 interstitial lung disease 57 encephalitis inflammation 57 Malignancies 57 neurological illnesses 57 clotting disorder 57 hematologic diseases 57 nephritis 57 RPLS 57 progressive degeneration 57 neurodevelopmental disorder 57 Creutzfeldt Jakob 57 Idiopathic 57 dermatomyositis 57 myopathy 57 haemorrhagic 57 Peripheral neuropathy 57 Gene Mutation 57 endocrine disorder 57 hyperparathyroidism 57 Fragile X Syndrome 56 Genital herpes 56 non arteritic anterior ischemic 56 leukemia ALL 56 DiGeorge syndrome 56 rheumatoid arthritis lupus 56 Periodontitis 56 juvenile idiopathic arthritis 56 polyneuropathy 56 phenylketonuria PKU 56 bone deformities 56 infantile spasms 56 rheumatic disease 56 Hyperglycemia 56 Joubert syndrome 56 chronic neurological disorder 56 Autoimmune diseases 56 adrenal insufficiency 56 congenital disorders 56 Idiopathic Pulmonary Fibrosis 56 sensory neuropathy 56 CMV infection