Related by context. Frequent words. (Click for all words.) 83 granted Orphan Drug 77 orphan drug 76 granted Fast Track 72 orphan medicinal product 69 Orphan Drug designation 68 Orphan Drug Designation 65 Orphan Drug 60 Fast Track Designation 59 Fast Track designation 59 investigational compound 59 Priority Review 57 Everolimus 56 relapsing forms 56 Satraplatin 56 Perifosine 55 humanized monoclonal antibody 55 ATryn R 54 Cladribine Tablets 54 Torisel 54 investigational drug 53 injectable formulation 53 orally administered 53 European Medicines Evaluation 53 Phenoptin 53 BAY #-# 53 Aclasta 53 Nimotuzumab 53 Jevtana 53 davunetide 53 oncology indications 52 Bevacizumab 52 investigational 52 6R BH4 52 diabetic neuropathic pain 52 opioid induced constipation 52 temsirolimus 52 Cimzia ® 52 antisense drug 51 orally bioavailable 51 tamibarotene 51 cutaneous T cell 51 Marketing Authorization Application 51 satraplatin 51 Marketing Authorization 51 Monotherapy 51 Rhucin ® 51 anticancer agent 51 potent inhibitor 50 Marqibo 50 BENLYSTA 50 VPRIV 50 HIV protease inhibitor 50 clofarabine 50 VIDAZA 50 Pixantrone 50 ThermoDox ® 50 gastrointestinal stromal tumors 50 relapsed multiple myeloma 50 Clolar 50 Sprycel 50 prodrug 50 Dupuytren contracture 50 pulmonary arterial hypertension PAH 49 methylnaltrexone 49 ambrisentan 49 FTY# 49 TORISEL 49 TREANDA 49 Treanda 49 administered orally 49 vandetanib 49 perifosine 49 biologic therapy 49 SUTENT 49 HDAC inhibitor 49 Amigal 49 Riquent 49 Bronchitol 49 Cimzia 49 XGEVA 49 ankylosing spondylitis 48 Avastin bevacizumab 48 Gencaro 48 MGCD# [001] 48 talactoferrin 48 Yondelis 48 Esbriet 48 Leukine 48 Naglazyme 48 Increlex 48 myelodysplastic syndromes MDS 47 Kuvan 47 carfilzomib 47 Zerenex 47 Saphris 47 cladribine 47 Yervoy 47 eltrombopag 47 AP# [003] 47 tocilizumab 47 ustekinumab