Related by context. Frequent words. (Click for all words.) 67 TTR amyloidosis 67 Parkinson disease multiple sclerosis 65 inflammatory bowel 65 commercializes innovative biopharmaceuticals 65 progressive degenerative 65 rheumatoid arthritis lupus 64 Pulmonary hypertension 64 neuro degenerative diseases 63 Parkinson disease Alzheimer disease 63 endocrine diseases 62 neurovascular diseases 62 immunodeficiencies 62 fatal neurodegenerative 62 blindness deafness 62 arthritis gout 62 meningitis encephalitis 62 cerebral palsy epilepsy 62 cerebral vascular disease 62 degenerative neurological disease 61 degenerative nerve 61 lupus erythematosus 61 neurogenic bladder 61 Becker muscular dystrophy 61 gastrointestinal mucositis 61 Fatty liver 61 chronic relapsing 60 neuromuscular dysfunction 60 Viral infections 60 degenerative disorders 60 immunologic diseases 60 cerebral palsy autism 60 autoimmune thyroid 60 Coeliac disease 60 Amyotrophic lateral sclerosis ALS 59 cholestasis 59 BioMarin develops 59 meningitis pneumonia 59 Pompe Disease 59 multiple sclerosis Parkinson disease 59 degenerative disorder 59 epidermolysis bullosa 59 mental retardation cerebral palsy 59 uremia 59 Medulloblastoma 59 multiple sclerosis rheumatoid arthritis 58 cognitive impairment associated 58 diabetes insipidus 58 motor neurone 58 rheumatoid arthritis multiple sclerosis 58 encephalitis meningitis 58 rheumatoid arthritis psoriasis 58 Psoriatic arthritis 58 pernicious anemia 58 chronic obstructive lung 58 Chronic inflammation 58 multiple sclerosis spinal cord 58 inflammation autoimmune diseases 58 unknown etiology 58 blood clotting disorder 58 rheumatic disease 58 Amyotrophic lateral sclerosis 58 retinitis pigmentosa RP 58 mastocytosis 58 lysosomal storage diseases 58 commercial bioproduction 58 myelodysplasia 58 pemphigus vulgaris 58 rheumatoid arthritis Crohn disease 58 cancer inflammation autoimmune 58 Joubert syndrome 58 motor neuron diseases 58 Chronic fatigue 58 myotonic dystrophy 58 bladder dysfunction 58 Irritable bowel syndrome 57 autoimmune disorders asthma 57 bone deformities 57 chronic inflammatory bowel 57 lung fibrosis 57 pulmonary emphysema 57 lifethreatening 57 leaky gut 57 chronic degenerative 57 demyelinating disease 57 Long QT syndrome 57 Cockayne Syndrome 57 Atopic dermatitis 57 SSc 57 Endometrial cancer 57 osteoarthritis rheumatoid arthritis 57 neurodegenerative disorder 57 muscular dystrophies 57 vascular abnormalities 57 Diabetes mellitus 57 interstitial cystitis IC 57 Pervasive Developmental Disorder 57 Spasticity 57 coagulation disorders 57 Hyperthyroidism 57 degenerative nerve disease 57 thyroiditis