Related by context. Frequent words. (Click for all words.) 68 lysosomal storage disorders 63 Panzem R 63 immuno inflammatory diseases 62 non alcoholic steatohepatitis 62 sodium Injection 60 R sorafenib tablets 59 MEK inhibitor 59 BioMarin develops 59 commercializes innovative biopharmaceuticals 58 systemic lupus erythematosus SLE 58 polymerase inhibitors 58 investigational compounds 58 fatal neurodegenerative 58 Amigal 58 myeloproliferative disorders 58 liposomal formulation 57 hematologic diseases 57 immunological disorders 57 phosphoinositide 3 57 short interfering RNA 57 nonsense mutation 56 preclinical compounds 56 Aurora kinase 56 endocrine diseases 56 muscular dystrophies 56 nicotinic alpha 7 56 Onalta 56 hypoxia inducible factor 55 myelodysplastic syndromes MDS 55 ALN TTR# 55 organ transplant rejection 55 HCV protease inhibitor 55 secondary hyperparathyroidism 55 otelixizumab 55 Multiple sclerosis MS 55 hypoparathyroidism 55 inflammatory autoimmune 55 dependent cellular cytotoxicity 55 viral hemorrhagic fevers 55 hematological malignancies 55 potently silencing specific 55 diabetic nephropathy 55 phase IIb clinical 55 ophthalmic diseases 54 rheumatoid arthritis multiple sclerosis 54 FGFR 54 chronic lymphocytic leukemia CLL 54 mixed dyslipidemia 54 Duchenne muscular dystrophy DMD 54 hematologic cancers 54 commercializing therapeutic 54 Parkinson disease Alzheimer disease 54 osteoarthritis rheumatoid arthritis 54 #ME# 54 anticancer compounds 54 neurodegenerative disorder 54 phenylketonuria PKU 54 autoimmune inflammatory 53 immunologic diseases 53 atacicept 53 Gaucher Disease 53 xenograft models 53 humanized monoclonal antibody 53 familial hypercholesterolemia 53 EGFR inhibitors 53 SGLT2 53 peroxisome proliferator activated 53 ZFP Therapeutic 53 anticancer compound 53 humanized anti 53 therapeutic monoclonal antibodies 53 proteasome inhibitors 53 squalamine 53 Periodontal disease 53 hepatitis C HCV 53 medulloblastomas 53 thyroid tumors 53 microRNA therapeutics 53 nonsense mutations 53 hematological cancers 52 Human Papilloma Virus HPV 52 lung adenocarcinoma 52 Sym# 52 FLT3 52 colorectal cancer CRC 52 TLR7 52 fibrotic diseases 52 multiple sclerosis rheumatoid arthritis 52 custirsen 52 RNAi therapeutic 52 phenylketonuria 52 cell lymphomas 52 cytomegalovirus CMV 52 pro inflammatory cytokines 52 progressive degeneration 52 Hepatitis C virus HCV 52 Alzheimer disease epilepsy 52 GRN#L 52 chemokines 52 antiviral compounds 52 small molecule inhibitors