Related by context. Frequent words. (Click for all words.) 75 orphan medicinal product 74 orphan drug 74 Orphan Drug status 71 orphan designation 71 Orphan Drug Designation 70 Orphan Drug designation 66 granted Orphan Drug 65 granted orphan 65 Fast Track Designation 62 ADVEXIN 62 Nimotuzumab 62 Elesclomol 62 refractory Hodgkin lymphoma 61 Pixantrone 61 Oncology Drug 61 Everolimus 61 Fast Track designation 61 oncology indications 60 Torisel 60 Perifosine 60 Priority Review 60 Marketing Authorization 60 Bevacizumab 60 Marketing Authorization Application 59 gastrointestinal stromal tumors 59 Orphan Products 59 humanized monoclonal antibody 59 biologic therapy 59 Rivaroxaban 59 Ceftobiprole 59 investigational 58 Dupuytren contracture 58 MGCD# [001] 58 Phenoptin 58 Sorafenib 58 alvimopan 58 Cladribine Tablets 58 TORISEL 58 cutaneous T cell 58 Clolar 57 investigational compound 57 GI GVHD 57 BAY #-# 57 pulmonary arterial hypertension PAH 57 Monoclonal Antibody 57 anticancer agent 57 Satraplatin 57 Drug Candidate 57 ThermoDox ® 57 Avastin bevacizumab 57 clofarabine 57 European Medicines Evaluation 57 eltrombopag 57 Vasovist 57 ONSOLIS 56 Gencaro 56 Friedreich Ataxia 56 Ceplene 56 ATryn R 56 TYKERB 56 FTY# 56 autoimmune indications 56 6R BH4 56 tezampanel 56 Small Molecule 56 granted Fast Track 56 Rare Diseases 56 humanized anti 56 Tygacil 56 injectable formulation 56 tamibarotene 56 Abstral 56 Phase III Trial 56 diabetic neuropathic pain 56 Rheumatoid Arthritis 56 Rifaximin 56 Bortezomib 56 Peramivir 55 BENLYSTA 55 relapsing forms 55 methylnaltrexone 55 Cimzia ® 55 Actemra 55 Naglazyme 55 taliglucerase alfa 55 Rituximab 55 Yondelis 55 Acute Myeloid Leukemia AML 55 lubiprostone 54 Marketing Authorization Application MAA 54 Loramyc ® 54 Kuvan 54 Jevtana 54 VEGF Trap 54 Sprycel 54 tocilizumab 54 Cetuximab 54 Acute Myeloid Leukemia 54 PROMACTA 54 TREANDA 54 VIDAZA