Related by context. Frequent words. (Click for all words.) 78 orphan designation 78 Orphan Drug status 75 Orphan Drug 75 orphan drug 74 Orphan Drug Designation 74 Orphan Drug designation 72 granted orphan 71 Orphan Medicinal Products 70 granted Orphan Drug 68 Marketing Authorization 67 Torisel 66 Fast Track Designation 65 Icatibant 65 European Medicines Evaluation 64 Marketing Authorization Application 64 Phenoptin 64 alvimopan 64 Fast Track designation 64 Everolimus 64 relapsing forms 64 Vimpat ® 64 TORISEL 64 VIDAZA 63 Jevtana 63 Ilaris 63 Rhucin ® 63 biologic therapy 63 Nexavar ® 63 PROMACTA 63 ATryn R 62 methylnaltrexone 62 tocilizumab 62 VPRIV 62 pulmonary arterial hypertension PAH 62 refractory Hodgkin lymphoma 62 Priority Review 62 Increlex 62 cutaneous T cell 61 BENLYSTA 61 TREANDA 61 CHMP opinion 61 Cethrin 61 Multaq R 61 injectable formulation 61 investigational compound 61 maribavir 61 clofarabine 61 bazedoxifene 61 GI GVHD 61 tamibarotene 61 granted Fast Track 61 Rhucin 61 Aclasta 60 eltrombopag 60 Ceplene 60 Cladribine Tablets 60 TYKERB 60 chronic angina 60 Marketing Authorization Application MAA 60 Keppra ® 60 Naglazyme 60 roflumilast 60 Zelrix 60 Avastin bevacizumab 60 Pixantrone 60 gastrointestinal stromal tumors 60 Nimotuzumab 60 velaglucerase alfa 60 Alemtuzumab 60 Cimzia ® 60 humanized anti 60 azacitidine 60 ADVEXIN 60 Clolar 59 Toctino ® 59 CHMP 59 davunetide 59 Amigal 59 Arixtra 59 Acute Myeloid Leukemia AML 59 Loramyc ® 59 Ceplene R 59 REVLIMID R 59 BAY #-# 59 Advexin 59 ELAPRASE 59 Esbriet 59 relapsed refractory multiple myeloma 59 metastatic renal cell carcinoma 59 pralatrexate 59 romidepsin 58 Dupuytren contracture 58 Tygacil 58 6R BH4 58 Ceftobiprole 58 thymalfasin 58 ThermoDox ® 58 fingolimod 58 humanized monoclonal antibody 58 Vasovist 58 talactoferrin